A light of hope for people suffering from intractable diseases
We are a biotechnology company from The University of Tokyo that specializes in research and development of genetic medicine to treat rare neuromuscular diseases. We are aiming to provide patients worldwide with medicines that enable fundamental treatment for these diseases.
To achieve true social reintegration for the bedridden and wheelchair-bounded patients
so that more active lifestyle can be taken and be enjoyed.
To enable more than only “life-sustaining treatment” offered by conventional medicines
to expedite the development of safe and effective new drugs
and delivering them to the bedside of suffering patients as soon as possible.
To offer the recovery that the joy in life
and the meaning of life can be found through medication.
These are our objectives we strive to achieve.
Genetic diseases that affect muscles and the nerve system
More than 100,000 people are suffering from a type of mitochondrial diseases. In spite of that, in modern medicine to this date, no effective cure has been developed for this disease.
Duchenne Muscular Dystrophy
More than 200,000 people are suffering from this disease
Muscle cells are damaged more rapidly than usual as muscles contract and extend. Suffering patients ultimately lead to death from respiratory or cardiac failure caused by protracted damage of muscle cells.
Developing new curative molecules
Mitochondrial diseases and muscular dystrophy are said to be rare intractable diseases. In fact, there are many kinds of intractable diseases which patients have been suffering from.
Our company, in order for the patients of intractable diseases to live normally just as anyone else, we have been continuing our research and development over 15 years.
Let us bring the light of hope to those who are suffering from intractable diseases
Developing a new drug is a costly operation. Your generous support will be vital in our research and development efforts.